- Investing.com
Gene Therapy Pionee | REGENXBIO's innovative AAV platform targets genetic and rare diseases, with promising developments in DMD, wet AMD, and MPS II treatments |
DMD Market Potential | Explore REGENXBIO's RGX-202 gene therapy for Duchenne muscular dystrophy, offering higher expression levels and broader patient eligibility than competitors |
Ocular Breakthroughs | Delve into REGENXBIO's partnership with AbbVie for ocular gene therapies, with pivotal trials and BLA submissions expected in the near future |
Financial Outlook | Analyst price targets range from $13 to $52, suggesting significant upside potential despite current unprofitability and a market cap of $487 million |
Metrics to compare | RGNX | Sector Sector - Average of metrics from a broad group of related Healthcare sector companies | Relationship RelationshipRGNXPeersSector | |
|---|---|---|---|---|
P/E Ratio | −2.2x | −3.8x | −0.5x | |
PEG Ratio | −0.12 | −0.09 | 0.00 | |
Price/Book | 4.2x | 2.4x | 2.6x | |
Price / LTM Sales | 2.5x | 10.9x | 3.2x | |
Upside (Analyst Target) | 221.4% | 142.2% | 50.8% | |
Fair Value Upside | Unlock | 8.3% | 7.7% | Unlock |
REGENXBIO Inc., a clinical-stage biotechnology company, provides gene therapies that deliver functional genes to cells with genetic defects in the United States. Its gene therapy product candidates are based on NAV Technology Platform, a proprietary adeno-associated virus gene delivery platform. The company’s products in pipeline includes ABBV-RGX-314 for the treatment of wet age-related macular degeneration, diabetic retinopathy, and other chronic retinal diseases; and RGX-202 for the treatment of Duchenne muscular dystrophy, as well as RGX-121 for the treatment of mucopolysaccharidosis type II. It also develops RGX-111 for the treatment of mucopolysaccharidosis type I. In addition, the company licenses its NAV Technology Platform to other biotechnology and pharmaceutical companies. Further, it has a collaboration and license agreement with AbbVie Global Enterprises Ltd. to develop ABBV-RGX-314 and with Nippon Shinyaku Co., Ltd. to develop RGX-121 and RGX-111 outside the United States. REGENXBIO Inc. was incorporated in 2008 and is headquartered in Rockville, Maryland.